Wednesday, August 29, 2012

A little unsettling

If you have kept up with CF research in the past couple of months, you know it has taken us on an emotional roller coaster. With the development of Kalydeco, a drug used to counteract the effects of Cystic Fibrosis in patients with a specific mutation, much hope has been bestowed on the CF community. Currently, clinical trials are being done with a combination of medicines to treat the cause of CF in patients with the most common mutation.

Well, the FDA has recently asked Vertex Pharmaceutical Company (the company that makes Kalydeco) to conduct a study to check for possible additional risks to taking the medicine. In a lab study, juvenile rats treated with Kalydeco developed cataracts. Although this problem did not occur in humans during their studies, the FDA is requesting further testing to be done. Right now, it is still recommended that patients using Kalydeco continue with their medical regimen until further data and information is provided. Click on this link to see the story on the Cystic Fibrosis Foundation website.

I wish the race for the cure was going absolutely perfectly and efficiently. I wish I could be part of one of these historic studies. I wish I was cured right now! But for now, I am going to have to trust God and learn the act of patience. What a hard art to learn...


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